17.12.22
Margaux discovering the world thanks to gene therapy
She was the first Belgian girl with the rare immunodeficiency ADA-SCID treated with the gene therapy approach developed by Telethon researchers. From the risk of a life of seclusion, she has conquered the possibility of doing whatever she likes.
31.05.22
In Italy for love and by choice
The story of Attya and her personal and professional journey that took her to the San Raffaele Telethon Institute for Gene Therapy in Milan.
10.10.19
Lorenzo wants to go far
“I can’t walk”. When you hear those words on the lips of a child below the age of three, it’s hard to turn your back and walk away. Imagine you’re the child’s parents. The words came out with the composed calmness of a fact of nature.
28.02.24
Fondazione Telethon announces commitment to make gene therapy for Wiskott-Aldrich syndrome available to patients
On the eve of the 26th World Rare Disease Day, Fondazione Telethon announces its commitment to ensure that gene therapy for Wiskott-Aldrich syndrome (WAS), a rare genetic disease of the immune system, will be available in the next future.
12.09.23
Fondazione Telethon and Orchard Therapeutics complete transfer of marketing authorization of Strimvelis for ADA-SCID in Europe
Una nuova sfida per Telethon, che amplia i confini della propria missione
20.04.23
Fondazione Cariplo and Fondazione Telethon: 21 projects funded with 5 million euros for basic research in rare diseases
The best projects of the 2022 call for basic research from all over Italy to study still obscure portions of our genetic heritage have been funded. The collaboration between Fondazione Cariplo and Fondazione Telethon continues: 21 new basic research projects have been funded for a total of about 5 million euros. The goal of the […]
